About Us

At Alexion, we work to help rare disease patients and the healthcare professionals who care for them.

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Alexion, AstraZeneca Rare Disease, is the rare disease focused group within AstraZeneca and was formed following the acquisition of Alexion Pharmaceuticals, Inc. in 2021. As a leader in the field of rare diseases, Alexion has been focused for almost 30 years dedicated to serving patients and families affected by rare and serious diseases through the discovery, development and commercialization of life-changing medicines.

Alexion’s research is focused on novel molecules and targets in the complement cascade, with particular focus on hematology, nephrology, neurology, metabolic disorders, cardiology, ophthalmology and acute care. Headquartered in Boston, Massachusetts, Alexion has offices around the world serving patients in more than 50 countries.

Moliner AM,Waligora J.The European Union Policy in the Field of Rare Diseases.2017.Adv Exp Med Biol;1031:561-587. doi: 10.1007/978-3-319-67144-4_30. Regulation (EC) No 536/2014 of the european parliament and of the council 0f 16 April 2014 on clinical trials on medicinal products for human use and repealing Directive 2001/20/EG.
Abrufbar unter: https://eur-lex.europa.eu/legal-content/DE/TXT/PDF/?uri=CELEX:32014R0536&from=EN